Xavier Liogier
Company: Loulou Foundation
Job title: Chief of Translational Science
Seminars:
Panel Discussion – How Can We Gain Consensus on Developing Patient Centric Outcome Measures for Rare Neurodevelopmental Indications? 11:00 am
day: Day Two
Leveraging Natural History Studies in Clinical Trial Design for Rare CNS and Neurodevelopmental Disorders 8:00 am
Despite common traits and symptoms, each NDD displays a high variability in their phenotype (e.g. ASD, Down syndrome, Rett syndrome, CDD) Characterizing this disease variability together with potential endpoints evaluation is critical before embarking into drug development Exploring case studies of how observational / natural history studies in NDD helped to improve early and late…Read more
day: Day Two