Preclinical Development of a Cross-Correcting Gene Therapy for CDKL5 Deficiency Disorder

Time: 3:30 pm
day: Day Two


  • Exploring preclinical research and development of gene therapies for the treatment of rare neurodevelopmental disorders, focusing on CDKL5
  • Evaluating pre-clinical data and efficacy in mice
  • Early developmental EEG and seizure phenotypes