How Do We Best Design Clinical Trials for Neurodevelopmental Disorders? A Clinical Researcher’s Perspective

Time: 10:10 am
day: Day One


• Important learnings from failed clinical trials in Fragile X Syndrome

• What changes have we made to these trials that have yielded positive results?

• How do we build relationships with communities that will lead to measurement of relevant outcomes in trials?

• What time constraints should we have on a clinical trial?

• What does a good clinical development program look like for neurodevelopmental disorders? What kinds of trials are needed?

• How should we manage recruitment and patient expectations for these trials?

• What do we need to know in order to develop appropriate tools for future clinical trials in each specific neurodevelopmental disorder?