About Event
Welcome to the 2nd Rare CNS & Neurodevelopmental Drug Development Summit
Returning in Boston for the second edition, the 2nd Rare CNS & Neurodevelopmental Drug Development Summit is the only meeting focused on advancing symptomatic and disease modifying treatments across rare genetic epilepsies and neurodevelopmental disorders.
Don’t miss out on the chance to unite with drug sponsors, researchers, foundations, and patient advocacy representatives to discuss case studies and lessons learned. This is the industry’s definitive opportunity to collaborate with patient groups and gain regulatory clarity on clinical trial design and endpoints, biomarkers and outcome measures, delivery and toxicity concerns.
This is your opportunity to:
Establish lasting connections with this dedicated community at the first ever-industry led meeting focused on advancing symptomatic and disease modifying treatments across neurodevelopmental disorders
Gain an important market update on the progress of neurodevelopmental drug development through pioneering clinical case studies leveraging diverse approaches across gene therapy, gene replacement, ASO’s and small molecules
Engage in critical discussions with world leading industry and academic experts and discover novel outcome measures that measure incremental change and how the industry is driving design innovation across disease specific clinical trials